410P GNT0004, Genethon's AAV8 vector-delivered microdystrophin gene therapy of Duchenne muscular dystrophy, first data of the phase I/II part of the GNT-016-MDYF all-in-one clinical trial in ambulant boys.

Autor: Laugel, V.1 (AUTHOR), De Lucia, S.2 (AUTHOR), Davion, J.3 (AUTHOR), Daniele, N.4 (AUTHOR), Cao, F.4 (AUTHOR), Sanz, M.4 (AUTHOR), Buscara, L.4 (AUTHOR), Blaie, S.4 (AUTHOR), Thibaut, L.4 (AUTHOR), Sagot, M.4 (AUTHOR), Riviere, A.4 (AUTHOR), Creoff, E.4 (AUTHOR), Lelait, M.4 (AUTHOR), Valent, A.4 (AUTHOR), Perret, G.4 (AUTHOR), Braun, S.4 (AUTHOR), Muntoni, F.5 (AUTHOR)
Zdroj: Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p.
Databáze: Academic Search Ultimate
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