An AAV capsid reprogrammed to bind human transferrin receptor mediates brain-wide gene delivery.

Autor: Qin Huang1, Chan, Ken Y.1, Wu, Jason1, Botticello-Romero, Nuria R.1, Qingxia Zheng1, Shan Lou1, Keyes, Casey1, Svanbergsson, Alexander1, Johnston, Jencilin1, Mills, Allan1, Chin-Yen Lin1, Brauer, Pamela P.1, Clouse, Gabrielle1, Pacouret, Simon1, Harvey, John W.1, Beddow, Thomas1, Hurley, Jenna K.1, Tobey, Isabelle G.1, Powell, Megan1, Chen, Albert T.1
Zdroj: Science. 6/14/2024, Vol. 384 Issue 6701, p1220-1227. 8p. 5 Graphs.
Databáze: Academic Search Ultimate