Long-Term Treatment of Gaucher Disease with Velaglucerase Alfa in ERT-Naïve Patients from the Gaucher Outcome Survey (GOS) Registry.

Autor: Deegan, Patrick1 (AUTHOR) patrick.deegan1@nhs.net, Lau, Heather2 (AUTHOR) heather.lau4@gmail.com, Elstein, Deborah3 (AUTHOR) debby.elstein@gmail.com, Fernandez-Sasso, Diego4 (AUTHOR) diegofernandezsasso@criocenter.com, Giraldo, Pilar5,6 (AUTHOR) giraldocastellano@gmail.com, Hughes, Derralynn7 (AUTHOR) derralynnhughes@nhs.net, Zimran, Ari8,9 (AUTHOR) azimran@gmail.com, Istaiti, Majdolen8 (AUTHOR) joleenist@szmc.org.il, Gadir, Noga3 (AUTHOR) noga.gadir-david@takeda.com, Botha, Jaco3 (AUTHOR) jaco.botha@takeda.com, Revel-Vilk, Shoshana8,9 (AUTHOR) srevelvilk@gmail.com
Zdroj: Journal of Clinical Medicine. May2024, Vol. 13 Issue 10, p2782. 16p.
Databáze: Academic Search Ultimate
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