AAV-Mediated CAG-Targeting Selectively Reduces Polyglutamine-Expanded Protein and Attenuates Disease Phenotypes in a Spinocerebellar Ataxia Mouse Model.

Autor: Niewiadomska-Cimicka, Anna1 (AUTHOR) lorraine.fievet@hotmail.fr, Fievet, Lorraine1 (AUTHOR) keime@igbmc.fr, Surdyka, Magdalena2 (AUTHOR) msurdyka@ibch.poznan.pl, Jesion, Ewelina2 (AUTHOR) jesion.ewelina@gmail.com, Keime, Céline1 (AUTHOR) virly@igbmc.fr, Singer, Elisabeth3,4,5 (AUTHOR) elisabeth.singer@med.uni-tuebingen.de, Eisenmann, Aurélie1 (AUTHOR), Kalinowska-Poska, Zaneta2 (AUTHOR) zkalinowska@ibch.poznan.pl, Nguyen, Hoa Huu Phuc5 (AUTHOR), Fiszer, Agnieszka6 (AUTHOR) agnieszka.fiszer@ibch.poznan.pl, Figiel, Maciej2 (AUTHOR) mfigiel@ibch.poznan.pl, Trottier, Yvon1 (AUTHOR) ania.niewiadomska@gmail.com
Zdroj: International Journal of Molecular Sciences. Apr2024, Vol. 25 Issue 8, p4354. 21p.
Databáze: Academic Search Ultimate
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