Real life data: follow-up assessment on Spanish Gaucher disease patients treated with eliglustat. TRAZELGA project.

Autor: Serrano-Gonzalo, Irene1,2 (AUTHOR), de Frutos, Laura López1,3 (AUTHOR), Lahoz-Gil, Carlos1 (AUTHOR), Delgado-Mateos, Francisco3,4 (AUTHOR), Fernández-Galán, María Ángeles3,5 (AUTHOR), Morales-Conejo, Montserrat6 (AUTHOR), Calle-Gordo, María Victoria3,7 (AUTHOR), Ibarretxe-Gerediaga, Daiana8 (AUTHOR), Madinaveitia-Ochoa, Andrés9 (AUTHOR), Albarracin-Arraigosa, Antonio10 (AUTHOR), Balanzat-Muñoz, José3,11 (AUTHOR), Correcher-Medina, Patricia12 (AUTHOR), García-Frade, Luis Javier3,13 (AUTHOR), Hernández-Rivas, Jesús María3,14 (AUTHOR), Labbadia, Francesca3,15 (AUTHOR), López-Dupla, Jesus Miguel16 (AUTHOR), Lozano-Almela, María Luisa3,17 (AUTHOR), Mora-Casterá, Elvira3,18 (AUTHOR), Noya-Pereira, María Soledad3,19 (AUTHOR), Ruíz-Guinaldo, María Ángeles3,20 (AUTHOR)
Zdroj: Orphanet Journal of Rare Diseases. 12/15/2023, Vol. 18 Issue 1, p1-12. 12p.
Databáze: Academic Search Ultimate
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