The L467F-F508del Complex Allele Hampers Pharmacological Rescue of Mutant CFTR by Elexacaftor/Tezacaftor/Ivacaftor in Cystic Fibrosis Patients: The Value of the Ex Vivo Nasal Epithelial Model to Address Non-Responders to CFTR-Modulating Drugs.

Autor: Sondo, Elvira1 (AUTHOR) elvirasondo@gaslini.org, Cresta, Federico2 (AUTHOR) federicocresta@gaslini.org, Pastorino, Cristina3 (AUTHOR) cristinapastorino22@gmail.com, Tomati, Valeria1 (AUTHOR) valeriatomati@gaslini.org, Capurro, Valeria1 (AUTHOR) valeriacapurro@gaslini.org, Pesce, Emanuela1 (AUTHOR) emanuela.pesce@yahoo.it, Lena, Mariateresa1 (AUTHOR) mariateresalena@gaslini.org, Iacomino, Michele1 (AUTHOR) micheleiacomino@gaslini.org, Baffico, Ave Maria4 (AUTHOR) avemariabaffico@gaslini.org, Coviello, Domenico4 (AUTHOR) domenicocoviello@gaslini.org, Bandiera, Tiziano5 (AUTHOR) tiziano.bandiera@iit.it, Zara, Federico1,3 (AUTHOR) federico.zara@unige.it, Galietta, Luis J. V.6,7 (AUTHOR) l.galietta@tigem.it, Bocciardi, Renata1,3 (AUTHOR) renata.bocciardi@unige.it, Castellani, Carlo2 (AUTHOR) carlocastellani@gaslini.org, Pedemonte, Nicoletta1 (AUTHOR) carlocastellani@gaslini.org
Zdroj: International Journal of Molecular Sciences. Mar2022, Vol. 23 Issue 6, p3175-3175. 15p.
Databáze: Academic Search Ultimate
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