Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria.
| Autor: | Balwani, M.1 manisha.balwani@mssm.edu, Sardh, E.2, Ventura, P.3, Peiro, P. A.4, Rees, D. C.5, Stolzel, U.6, Bissell, D. M.7, Bonkovsky, H. L.8, Windyga, J.9, Anderson, K. E.10, Parker, C.11, Silver, S. M.12, Keel, S. B.13, Wang, J.-D.14, Stein, P. E.5, Harper, P.2, Vassiliou, D.2, Wang, B.7, Phillips, J.11, Ivanova, A.15 |
|---|---|
| Zdroj: | New England Journal of Medicine. 6/11/2020, Vol. 382 Issue 24, p2289-2301. 13p. |
| Databáze: | Academic Search Ultimate |
| Externí odkaz: |
|