Cas9/gRNA targeted excision of cystic fibrosis-causing deep-intronic splicing mutations restores normal splicing of CFTR mRNA.

Autor: Sanz, David J.1, Hollywood, Jennifer A.1,2, Scallan, Martina F.2, Harrison, Patrick T.1 p.harrison@ucc.ie
Zdroj: PLoS ONE. 9/1/2017, Vol. 12 Issue 9, p1-13. 13p.
Databáze: Academic Search Ultimate