Short (16-mer) locked nucleic acid splice-switching oligonucleotides restore dystrophin production in Duchenne Muscular Dystrophy myotubes.

Autor: Pires, Vanessa Borges1, Simões, Ricardo1, Mamchaoui, Kamel2, Carvalho, Célia1, Carmo-Fonseca, Maria1 carmo.fonseca@medicina.ulisboa.pt
Zdroj: PLoS ONE. 7/24/2017, Vol. 12 Issue 7, p1-13. 13p.
Databáze: Academic Search Ultimate