Short (16-mer) locked nucleic acid splice-switching oligonucleotides restore dystrophin production in Duchenne Muscular Dystrophy myotubes.
Autor: | Pires, Vanessa Borges1, Simões, Ricardo1, Mamchaoui, Kamel2, Carvalho, Célia1, Carmo-Fonseca, Maria1 carmo.fonseca@medicina.ulisboa.pt |
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Zdroj: | PLoS ONE. 7/24/2017, Vol. 12 Issue 7, p1-13. 13p. |
Databáze: | Academic Search Ultimate |
Externí odkaz: |