Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study.

Autor:	Cirak S (AUTHOR), Arechavala-Gomeza V (AUTHOR), Guglieri M (AUTHOR), Feng L (AUTHOR), Torelli S (AUTHOR), Anthony K (AUTHOR), Abbs S (AUTHOR), Garralda ME (AUTHOR), Bourke J (AUTHOR), Wells DJ (AUTHOR), Dickson G (AUTHOR), Wood MJ (AUTHOR), Wilton SD (AUTHOR), Straub V (AUTHOR), Kole R (AUTHOR), Shrewsbury SB (AUTHOR), Sewry C (AUTHOR), Morgan JE (AUTHOR), Bushby K (AUTHOR), Muntoni F (AUTHOR)
Zdroj:	Lancet. 8/13/2011, Vol. 378 Issue 9791, p595-605. 11p.
Databáze:	Academic Search Ultimate
Externí odkaz:	Zobrazit plný text záznamu