Clinical outcomes of Hurler syndrome treated exclusively with enzyme replacement therapy from a young age.

Autor: Eisengart, Julie B.1, Shapiro, Elsa G.1, Rudser, Kyle D.1, Ahmed, Alia1, Kovac, Victor2, Delaney, Kathleen1, Mercer, Jean3, Jones, Simon3, Van der Ploeg, Ans4, Mengel, Karl-Eugen5, Goekce, Seyfullah5, Whitley, Chester B.1
Zdroj: Molecular Genetics & Metabolism. Feb2015, Vol. 114 Issue 2, pS40-S40. 1p.
Databáze: Academic Search Ultimate