In utero gene therapy rescues microcephaly caused by Pqbp1-hypofunction in neural stem progenitor cells.

Autor: Ito, H1, Shiwaku, H1, Yoshida, C1, Homma, H1, Luo, H1, Chen, X1, Fujita, K1, Musante, L2, Fischer, U2, Frints, S G M3, Romano, C4, Ikeuchi, Y5, Shimamura, T6, Imoto, S6, Miyano, S6, Muramatsu, S-i7, Kawauchi, T8, Hoshino, M9, Sudol, M10, Arumughan, A11
Zdroj: Molecular Psychiatry. Apr2015, Vol. 20 Issue 4, p459-471. 13p.
Databáze: Academic Search Ultimate