Long-Term Systemic Therapy of Fabry Disease in a Knockout Mouse by Adeno-Associated Virus-Mediated Muscle-Directed Gene Transfer

Autor: Takahashi, Hiroshi, Hirai, Yukihiko, Migita, Makoto, Seino, Yoshihiko, Fukuda, Yuh, Sakuraba, Hitoshi, Kase, Ryoichi, Kobayashi, Toshihide, Hashimoto, Yasuhiro, Shimada, Takashi
Zdroj: Proceedings of the National Academy of Sciences of the United States of America, 2002 Oct . 99(21), 13777-13782.
Databáze: JSTOR Journals