Nonclinical Safety Evaluation of scAAV8-RLBP1 for Treatment of RLBP1 Retinitis Pigmentosa

Autor: MacLachlan, Timothy K., Milton, Mark N., Turner, Oliver, Tukov, Francis, Choi, Vivian W., Penraat, Jan, Hanks, Shawn M., Vrouvlianis, Joanna, Leehy, Barrett, Li, Hui, Delmotte, Marie-Hélène, Michaut, Lydia, Jaffee, Bruce D., Bigelow, Chad E.
Zdroj: In Molecular Therapy - Methods & Clinical Development 16 March 2018 8:105-120
Databáze: ScienceDirect