Improved MECP2 Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery

Autor: Sinnett, Sarah E., Hector, Ralph D., Gadalla, Kamal K.E., Heindel, Clifford, Chen, Daphne, Zaric, Violeta, Bailey, Mark E.S., Cobb, Stuart R., Gray, Steven J.
Zdroj: In Molecular Therapy - Methods & Clinical Development 16 June 2017 5:106-115
Databáze: ScienceDirect