Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency
| Autor: | Pham, Vi, Tricoli, Lucas, Hong, Xinying, Wongkittichote, Parith, Castruccio Castracani, Carlo, Guerra, Amaliris, Schlotawa, Lars, Adang, Laura A., Kuhs, Amanda, Cassidy, Margaret M., Kane, Owen, Tsai, Emily, Presa, Maximiliano, Lutz, Cathleen, Rivella, Stefano B., Ahrens-Nicklas, Rebecca C. |
|---|---|
| Zdroj: | In Molecular Therapy 6 November 2024 32(11):3829-3846 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|