α-L-iduronidase fused with humanized anti-human transferrin receptor antibody (lepunafusp alfa) for mucopolysaccharidosis type I: A phase 1/2 trial

Autor:	Harmatz, Paul, Giugliani, Roberto, Martins, Ana Maria, Hamazaki, Takashi, Kubo, Toru, Kira, Ryutaro, Minami, Kohtaro, Ikeda, Toshiaki, Moriuchi, Hiroaki, Kawashima, Satoshi, Takasao, Naoko, So, Sairei, Sonoda, Hiroyuki, Hirato, Tohru, Tanizawa, Kazunori, Schmidt, Mathias, Sato, Yuji
Zdroj:	In Molecular Therapy 6 March 2024 32(3):609-618
Databáze:	ScienceDirect
Externí odkaz:	Zobrazit plný text záznamu