Highly Efficient Gene Editing of Cystic Fibrosis Patient-Derived Airway Basal Cells Results in Functional CFTR Correction

Autor: Suzuki, Shingo, Crane, Ana M., Anirudhan, Varada, Barillà, Cristina, Matthias, Nadine, Randell, Scott H., Rab, Andras, Sorscher, Eric J., Kerschner, Jenny L., Yin, Shiyi, Harris, Ann, Mendel, Matthew, Kim, Kenneth, Zhang, Lei, Conway, Anthony, Davis, Brian R.
Zdroj: In Molecular Therapy 8 July 2020 28(7):1684-1695
Databáze: ScienceDirect