Codon-Optimized RPGR Improves Stability and Efficacy of AAV8 Gene Therapy in Two Mouse Models of X-Linked Retinitis Pigmentosa
| Autor: | Fischer, M. Dominik, McClements, Michelle E., Martinez-Fernandez de la Camara, Cristina, Bellingrath, Julia-Sophia, Dauletbekov, Daniyar, Ramsden, Simon C., Hickey, Doron G., Barnard, Alun R., MacLaren, Robert E. |
|---|---|
| Zdroj: | In Molecular Therapy 2 August 2017 25(8):1854-1865 |
| Databáze: | ScienceDirect |
| Externí odkaz: |
|