Long-term Restoration of Cardiac Dystrophin Expression in Golden Retriever Muscular Dystrophy Following rAAV6-mediated Exon Skipping

Autor: Bish, Lawrence T, Sleeper, Meg M, Forbes, Sean C, Wang, Bingjing, Reynolds, Caryn, Singletary, Gretchen E, Trafny, Dennis, Morine, Kevin J, Sanmiguel, Julio, Cecchini, Sylvain, Virag, Tamas, Vulin, Adeline, Beley, Cyriaque, Bogan, Janet, Wilson, James M, Vandenborne, Krista, Kornegay, Joe N, Walter, Glenn A, Kotin, Robert M, Garcia, Luis, Sweeney, H Lee
Zdroj: In Molecular Therapy March 2012 20(3):580-589
Databáze: ScienceDirect