COMET post hoc analysis: Efficacy of long-term avalglucosidase alfa in subgroups of participants with late-onset Pompe disease
| Autor: | Toscano, Antonio, Kishnani, Priya, Dimachkie, Mazen M., Sacconi, Sabrina, Van der Beek, Nadine, Roberts, Mark E., Suwazono, Shugo, Choi, Young Chul, de Souza, Paulo Victor Sgobbi, Schoser, Benedikt, Armstrong, Nicole, Huynh-Ba, Olivier, Thibault, Nathan, Periquet, Magali, Diaz-Manera, Jordi |
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| Zdroj: | In Molecular Genetics and Metabolism February 2024 141(2) |
| Databáze: | ScienceDirect |
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