Long-term inhibition of glycosphingolipid accumulation in Fabry model mice by a single systemic injection of AAV1 vector in the neonatal period

Autor: Ogawa, Koichi, Hirai, Yukihiko, Ishizaki, Masamichi, Takahashi, Hiroshi, Hanawa, Hideki, Fukunaga, Yoshitaka, Shimada, Takashi
Zdroj: In Molecular Genetics and Metabolism 2009 96(3):91-96
Databáze: ScienceDirect