The experience of clinical study and trial participation in rare diseases: A scoping review of centronuclear myopathy and other neuromuscular disorders

Autor: Stinissen, Lizan, Bouma, Sietse, Böhm, Johann, van Tienen, Jeno, Fischer, Holger, Hughes, Zak, Lennox, Anne, Ward, Erin, Wood, Marie, Foley, A. Reghan, Oortwijn, Wija, Jungbluth, Heinz, Voermans, Nicol C.
Zdroj: In Neuromuscular Disorders May 2024 38:1-7
Databáze: ScienceDirect