P49 The efficacy and safety of Tideglusib in a randomized, placebo-controlled, double blind study in children and adolescents with congenital myotonic dystrophy (REACH CDM study)

Autor: Horrigan, J., Snape, M., Fantelli, E.
Zdroj: In Neuromuscular Disorders October 2023 33 Supplement 1:S70-S71
Databáze: ScienceDirect