P.126 Genotype-unmatched controls are feasible for drug development in Duchenne muscular dystrophy (DMD)

Autor: Muntoni, F., Signorovitch, J., Frean, M., Fillbrunn, M., Sajeev, G., Ward, S., McDonald, C., Goemans, N., Niks, E., Wong, B., Servais, L., Straub, V., de Groot, I., Chesshyre, M., Tian, C., Manzur, A., Mercuri, E., Aartsma-Rus, A., Groups, Study
Zdroj: In Neuromuscular Disorders October 2022 32 Supplement 1:S100-S100
Databáze: ScienceDirect