P.105 Safety and effectiveness of onasemnogene abeparvovec (OA) alone or with other disease-modifying therapies (DMTs): Findings from RESTORE

Autor: Servais, L., Benguerba, K., De Vivo, D., Kirschner, J., Muntoni, F., Proud, C., Tizzano, E., Saito, K., Raju, D., LaMarca, N., Sun, R., Anderson, F., Faulkner, E., Finkel, R.
Zdroj: In Neuromuscular Disorders October 2022 32 Supplement 1:S87-S87
Databáze: ScienceDirect