Newborn Screening for Hurler Syndrome Facilitates Early Transplant and Good Outcomes
Autor: | Bauchat, Andrea, Stokhuyzen, Andre, Driscoll, Timothy A., Martin, Paul L., Kurtzberg, Joanne, Mahadeo, Kris M., Prasad, Vinod K. |
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Zdroj: | In Pediatric Neurology February 2025 163:21-26 |
Databáze: | ScienceDirect |
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