PS-196-Efficacy and safety of sebelipase alfa over 144 weeks in a diverse population of children and adults with lysosomal acid lipase deficiency

Autor: Burton, Barbara, Sanchez, Alejandra Consuelo, Kostyleva, Maria, Martins, Ana Maria, Marulkar, Sachin, Abel, Florian, Baric, Ivo
Zdroj: In Journal of Hepatology April 2019 70(1) Supplement:e121-e122
Databáze: ScienceDirect