Impact of high-dose, chemically modified sulfamidase on pathology in a murine model of MPS IIIA

Autor: Rozaklis, Tina, Beard, Helen, Hassiotis, Sofia, Garcia, Antony R., Tonini, Matthew, Luck, Amanda, Pan, Jing, Lamsa, Justin C., Hopwood, John J., Hemsley, Kim M.
Zdroj: In Experimental Neurology July 2011 230(1):123-130
Databáze: ScienceDirect