Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: A Global Phase 1 Study for Adult and Pediatric Patients
Autor: | López Lorenzo, José Luis *, Navarro, Susana *, Shah, Ami J, Roncarolo, Maria Grazia, Sevilla, Julián *, Llanos, Lucía *, Pérez Camino de Gaisse, Begoña *, Sanchez, Sol *, Glader, Bertil, Chien, May, Quintana Bustamante, Oscar *, Beard, Brian C *, Law, Kenneth M *, Zeini, Miriam *, Choi, Grace *, Nicoletti, Eileen *, Bueren, Juan A *, Rao, Gayatri R *, Schwartz, Jonathan D, Segovia, José C * |
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Zdroj: | In Blood 5 November 2020 136 Supplement 1:47-47 |
Databáze: | ScienceDirect |
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