Future therapies for cystic fibrosis

Autor: Lucy Allen, Lorna Allen, Siobhan B. Carr, Gwyneth Davies, Damian Downey, Marie Egan, Julian T. Forton, Robert Gray, Charles Haworth, Alexander Horsley, Alan R. Smyth, Kevin W. Southern, Jane C. Davies
Jazyk: angličtina
Rok vydání: 2023
Předmět:
Zdroj: Nature Communications, Vol 14, Iss 1, Pp 1-13 (2023)
Druh dokumentu: article
ISSN: 2041-1723
DOI: 10.1038/s41467-023-36244-2
Popis: The cystic fibrosis landscape has changed dramatically over the last few decades, with improvements in patient quality of life, prognosis and predicted survival. In part, this is related to the availability of novel CFTR modulator drugs, although prior advances in symptom-directed therapies and diagnosis had already led to substantial improvements. However, the authors, part of a national CF focused group, recognize that more needs to be done and outline their considerations on research priorities in this perspective.
Databáze: Directory of Open Access Journals