First-in-human study of a liver-directed AAV gene therapy (FLT190) in Fabry disease

Autor:	Azadeh Kia, Jey Jeyakumar, Niten Patel, Gerard Short, Romuald Corbau, Derralynn Hughes, Rose Sheridan, Amit C. Nathwani, Leanne Dronfield, Russell Kinch
Rok vydání:	2020
Předmět:	Endocrinology business.industry Endocrinology Diabetes and Metabolism Genetic enhancement Genetics Cancer research Medicine First in human business medicine.disease Molecular Biology Biochemistry Fabry disease
Zdroj:	Molecular Genetics and Metabolism. 129:S77-S78
ISSN:	1096-7192
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::f964e563397b7fad1a593ea0d5ed30f5 https://doi.org/10.1016/j.ymgme.2019.11.188 Zobrazit plný text záznamu Full Text from ScienceDirect