SUN-325 SAFETY AND EFFICACY OF LUMASIRAN, AN INVESTIGATIONAL RNA INTERFERENCE (RNAi) THERAPEUTIC, IN ADULT AND PEDIATRIC PATIENTS WITH PRIMARY HYPEROXALURIA TYPE 1

Autor:	Bernd Hoppe, Pierre Cochat, Dawn S. Milliner, Jaap W. Groothoff, W van't Hoff, Georges Deschênes, Jérôme Harambat, Daniella Magen, John C. Lieske, Sally-Anne Hulton, Yaacov Frishberg
Rok vydání:	2019
Předmět:	Primary hyperoxaluria Nephrology business.industry RNA interference medicine medicine.disease Bioinformatics business
Zdroj:	Kidney International Reports. 4:S295
ISSN:	2468-0249
DOI:	10.1016/j.ekir.2019.05.734
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::e0b7fb3edf3128ab29a1281663475931 https://doi.org/10.1016/j.ekir.2019.05.734 Zobrazit plný text záznamu