FIREFISH Part 2: 24-Month Efficacy and Safety of Risdiplam in Infants with Type 1 Spinal Muscular Atrophy (SMA)
Autor: | Maria Mazurkiewicz-Bełdzińska, Marianne Gerber, Heidemarie Kletzl, R. Masson, Andrea Klein, Edmar Zanoteli, Ksenija Gorni, Basil T. Darras, Kristy Rose, Giovanni Baranello, Laurent Servais, H. Xiong, D. Vlodavets, A. Dodman, M. El-Khairi, Renata S. Scalco |
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Rok vydání: | 2021 |
Předmět: | |
Zdroj: | Abstracts of the 46th Annual Meeting of the Society for Neuropediatrics. |
ISSN: | 1439-1899 |
DOI: | 10.1055/s-0041-1739636 |
Databáze: | OpenAIRE |
Externí odkaz: |