Safety, β-Sarcoglycan Expression, and Functional Outcomes from Systemic Gene Transfer of rAAVrh74.MHCK7.hSGCB in LGMD2E/R4
Autor: | Jerry R. Mendell, E. R. Pozsgai, Linda Lowes, S. Neuhaus, M. A. Iammarino, A. S. Meadows, Kelly J. Lehman, Danielle A. Griffin, N. F. Reash, E. Koenig, A. Mueller-York, Sarah Lewis, L. R. Rodino-Klapac, X. Li, Kathleen Church |
---|---|
Rok vydání: | 2021 |
Předmět: | |
Zdroj: | Abstracts of the 46th Annual Meeting of the Society for Neuropediatrics. |
ISSN: | 1439-1899 |
DOI: | 10.1055/s-0041-1739648 |
Databáze: | OpenAIRE |
Externí odkaz: |