Fanconi anemia and βc deficiency-associated pulmonary alveolar proteinosis as two hereditary diseases of childhood which are potentially curable by stem cell gene therapy but require different therapeutic approaches.

Autor: Dirksen, U., Moritz, T., Burdach, S., Flasshove, M., Hanenberg, H.
Zdroj: Klinische Pädiatrie; 1999, Vol. 211 Issue 4, p329-335, 7p
Databáze: Complementary Index