Consensus Guidelines for the Design and In Vitro Preclinical Efficacy Testing N-of-1 Exon Skipping Antisense Oligonucleotides.
| Autor: | Aartsma-Rus, Annemieke, Garanto, Alejandro, van Roon-Mom, Willeke, McConnell, Erin M., Suslovitch, Victoria, Yan, Winston X., Watts, Jonathan K., Yu, Timothy W. |
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| Zdroj: | Nucleic Acid Therapeutics; Jan2023, Vol. 33 Issue 1, p17-25, 9p |
| Databáze: | Complementary Index |
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