Enzyme replacement therapy interruption in mucopolysaccharidosis type IVA patients and its impact in different clinical outcomes.

Autor: Politei, Juan, Porras‐Hurtado, Gloria Liliana, Guelbert, Norberto, Fainboim, Alejandro, Horovitz, Dafne Dain Gandelman, Satizábal, José María
Zdroj: Journal of Inherited Metabolic Disease Reports; Mar2021, Vol. 58 Issue 1, p104-113, 10p
Databáze: Complementary Index
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