305 Development of an adenine base editing-based strategy to allow temporospatial control of correction of W1282X-CFTR.

Autor: Zollo, I. (AUTHOR), Santos, L. (AUTHOR), Alves, J. (AUTHOR), Harrison, P. (AUTHOR), Farinha, C. (AUTHOR)
Zdroj: Journal of Cystic Fibrosis. Sep2024 Supplement 2, Vol. 23, pS162-S162. 1p.
Databáze: Academic Search Ultimate