Clinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa.

Autor: Hughes, D.1 rmgvdah@ucl.ac.uk, Giugliani, R.2, Guffon, N.3, Jones, S. A.4, Mengel, K. E.5, Parini, R.6, Matousek, R.7, Hawley, S. M.7, Quartel, A.7
Zdroj: Orphanet Journal of Rare Diseases. 5/23/2017, Vol. 12, p1-8. 8p.
Databáze: Academic Search Ultimate