Pressure for drug development in lysosomal storage disorders - a quantitative analysis thirty years beyond the US orphan drug act.

Autor: Mechler, Konstantin1, Mountford, William K.2, Hoffmann, Georg F.3, Ries, Markus3 markus.ries@uni-heidelberg.de
Zdroj: Orphanet Journal of Rare Diseases. Apr2015, Vol. 10 Issue 1, p1-9. 9p.
Databáze: Academic Search Ultimate