A European pilot study in Dravet Syndrome to delineate what really matters for the patients and families

Autor: Nicole Chemaly, Mathieu Kuchenbuch, Théo Teng, Elodie Marie, Gianluca D'Onofrio, Tommaso Lo Barco, Isabella Brambilla, Silke Flege, Anne‐Sophie Hallet, Rima Nabbout

Publikováno v: Epilepsia Open, Vol 9, Iss 1, Pp 388-396 (2024)

Abstract We aimed to identify caregivers' opinions on the outcome measures that matter in clinical trials in individuals with Dravet syndrome (DS). We conducted a prospective European multicenter study based on an 11 closed questions survey developed

Externí odkaz: https://doaj.org/article/05f5880e27fe45268bf963808043bab8

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Putting non-alcoholic fatty liver disease on the radar for primary care physicians: how well are we doing?

Autor: Arun J. Sanyal

Publikováno v: BMC Medicine, Vol 16, Iss 1, Pp 1-3 (2018)

Abstract Non-alcoholic fatty liver disease (NAFLD) has emerged as a common cause of liver-related morbidity and mortality. Tackling this condition at a societal level will require a clear understanding of the burden of disease in the general populati

Externí odkaz: https://doaj.org/article/6aaccbe1d726498e897eef0a77bf5a72

A European pilot study in Dravet Syndrome to delineate what really matters for the patients and families

Autor: Elodie Marie, Rima Nabbout, Anne-Sophie Hallet, Tommaso Lo Barco, Gianluca D'Onofrio, Mathieu Kuchenbuch, Nicole Chemaly, Theo Teng, Silke Flege, Isabella Brambilla

We aimed to identify caregivers' opinions on the outcome measures that matter in clinical trials in individuals with Dravet syndrome (DS). We conducted a prospective European multicentre study based on a 11-closed questions' survey developed by the F

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8b3d2172bdb2eb03e8951588eea5e9e0
https://hdl.handle.net/11380/1290166

Perceptions of Oncologists, Healthcare Policy Makers, Patients and the General Population on the Value of Pharmaceutical Treatments in Oncology

Autor: Cristina Avendaño, José A. Sacristán, Luis Lizán, Pilar Garrido, M Comellas, Javier Espinosa, Tatiana Dilla, Juan J. Cruz-Hernández

Publikováno v: Repositori Universitat Jaume I
Universitat Jaume I
Advances in Therapy
Repositorio Institucional de la Consejería de Sanidad de la Comunidad de Madrid
Consejería de Sanidad de la Comunidad de Madrid

Introduction The purpose of this study was to explore the main factors explaining the relative weight of the different attributes that determine the value of oncologic treatments from the different perspectives of healthcare policy makers (HCPM), onc

Externí odkaz: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::8f0767cc1304b3c51333520d4b7ad7e5
https://doi.org/10.1007/s12325-016-0415-5