Zobrazeno 1 - 10
of 21
pro vyhledávání: '"cTAP"'
Autor:
Francesco Muntoni, James Signorovitch, Gautam Sajeev, Nicolae Done, Zhiwen Yao, Nathalie Goemans, Craig McDonald, Eugenio Mercuri, Erik H Niks, Brenda Wong, Krista Vandenborne, Volker Straub, Imelda J M de Groot, Cuixia Tian, Adnan Manzur, Ibrahima Dieye, Henry Lane, Susan J Ward, Laurent Servais, PRO-DMD-01 study investigators, Association Française contre les Myopathies, UK NorthStar Clinical Network, ImagingDMD investigators, cTAP
Publikováno v:
PLoS ONE, Vol 19, Iss 7, p e0304984 (2024)
Evaluations of treatment efficacy in Duchenne muscular dystrophy (DMD), a rare genetic disease that results in progressive muscle wasting, require an understanding of the 'meaningfulness' of changes in functional measures. We estimated the minimal de
Externí odkaz:
https://doaj.org/article/0cdc19d226b54599940b6eaa426e1e89
Autor:
ctapanya@yahoo.com, Sriwan Tapanya
Performance measurement is critical to achieving a firms objectives, translating strategy into action and monitoring progress. Selection of a performance measurement system involves a complex interplay between strategy, a firms internal and exter
Akademický článek
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Autor:
Nathalie Goemans, Brenda Wong, Marleen Van den Hauwe, James Signorovitch, Gautam Sajeev, David Cox, John Landry, Madeline Jenkins, Ibrahima Dieye, Zhiwen Yao, Intekhab Hossain, Susan J Ward, Collaborative Trajectory Analysis Project (cTAP)
Publikováno v:
PLoS ONE, Vol 15, Iss 6, p e0232870 (2020)
The timed 4-stair climb (4SC) assessment has been used to measure function in Duchenne muscular dystrophy (DMD) practice and research. We sought to identify prognostic factors for changes in 4SC, assess their consistency across data sources, and the
Externí odkaz:
https://doaj.org/article/a287b4457f924d48a566aa43b835a618
Autor:
Nathalie Goemans, Marleen Vanden Hauwe, James Signorovitch, Elyse Swallow, Jinlin Song, Collaborative Trajectory Analysis Project (cTAP)
Publikováno v:
PLoS ONE, Vol 11, Iss 10, p e0164684 (2016)
BackgroundDeficits in ambulatory function progress at heterogeneous rates among individuals with Duchenne muscular dystrophy (DMD). The resulting inherent variability in ambulatory outcomes has complicated the design of drug efficacy trials and cloud
Externí odkaz:
https://doaj.org/article/ba1deb34931b4ef4b0545210bcc27b5b
Autor:
N. Goemans, C. McDonald, J. Signorovitch, G. Sajeev, M. Fillbrunn, H. Wong, E. Mercuri, K. Vandenborne, F. Muntoni, S. Ward, The ImagingDMD study, null iMDEX, null cTAP
Publikováno v:
Neuromuscular Disorders. 30:S63-S64
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::39376a62a247535221106334b4882cde
https://doi.org/10.1016/j.nmd.2020.08.063
https://doi.org/10.1016/j.nmd.2020.08.063
Autor:
cTAP, Zhiwen Yao, M. Rabbia, R. Ong, Brenda Wong, I. Dieye, H. Staunton, James Signorovitch, Gautam Sajeev, S. Ward
Publikováno v:
Neuromuscular Disorders. 29:S106
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::b4b2e90e36bfc955e856c1d249ca5015
https://doi.org/10.1016/j.nmd.2019.06.251
https://doi.org/10.1016/j.nmd.2019.06.251
Akademický článek
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Autor:
Mercuri E1, Signorovitch JE2, Swallow E3, Song J3, Ward SJ4, DMD Italian Group, Trajectory Analysis Project (cTAP). * Pane M5, Mazzone E5, Messina S6, Vita GL6, Sormani MP7, D'Amico A8, Berardinelli A9, Magri F10, Comi GP11, Baranello G12, Mongini T13, Pini A14, Battini R15, Pegoraro E16, Bruno C17, Politano L18, Previtali S19, Binks MH20, Campion G21, Charnas L22, Kaye E23, Kelly M24, Morris C20, Reha A25.
High variability in patients' changes in 6 minute walk distance (6MWD) over time has complicated clinical trials of treatment efficacy in Duchenne muscular dystrophy (DMD). We assessed whether boys with DMD could be grouped into classes that shared s
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=od______3977::6146f4ff6f6d6e2c9446468ade6ebaf5
http://hdl.handle.net/11591/368477
http://hdl.handle.net/11591/368477
Akademický článek
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