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pro vyhledávání: '"Vyankat Sontakke"'
Autor:
Vignesh N. Hariharan, Takahiro Nakamura, Minwook Shin, Qi Tang, Vyankat Sontakke, Jillian Caiazzi, Samuel Hildebrand, Anastasia Khvorova, Ken Yamada
Publikováno v:
Molecular Therapy: Nucleic Acids, Vol 35, Iss 2, Pp 102230- (2024)
Small interfering RNAs (siRNAs) are revolutionizing the treatment of liver-associated indications. Yet, robust delivery to extrahepatic tissues remains a challenge. Conjugating lipids (e.g., docosanoic acid [DCA]) to siRNA supports extrahepatic deliv
Externí odkaz:
https://doaj.org/article/11b7081549e04a32bb58409f85966f34