Zobrazeno 1 - 10
of 64
pro vyhledávání: '"Tsai, SQ"'
Autor:
Costello, Joseph, Maeder, ML, Angstman, JF, Richardson, ME, Linder, SJ, Cascio, VM, Tsai, SQ, Ho, QH, Sander, JD, Reyon, D, Bernstein, BE
Publikováno v:
Costello, Joseph; Maeder, ML; Angstman, JF; Richardson, ME; Linder, SJ; Cascio, VM; et al.(2013). Targeted DNA demethylation and activation of endogenous genes using programmable TALE-TET1 fusion proteins. UC San Francisco: Retrieved from: http://www.escholarship.org/uc/item/8nz114dh
Genome-wide studies have defined cell type-specific patterns of DNA methylation that are important for regulating gene expression in both normal development and disease. However, determining the functional significance of specific methylation events
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=od_______325::cfb2940f89bd671049c08d8204539c0e
http://www.escholarship.org/uc/item/8nz114dh
http://www.escholarship.org/uc/item/8nz114dh
Autor:
Bzhilyanskaya V; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA., Ma L; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA 02114, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA 02114, USA.; Department of Pathology, Harvard Medical School, Boston, MA 02115, USA., Liu S; Molecular Cytogenetic Core Facility, Mouse Cancer Genetics Program, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Frederick, MD 21702, USA., Fox LR; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA 02114, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA 02114, USA., Whittaker MN; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA 02114, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA 02114, USA., Meis RJ; CELLSCRIPT, Madison, WI 53713, USA.; Wisconsin Institute for Immune and Cell Therapy (WIICT), Madison, WI 53713, USA., Choi U; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA., Lawson A; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA., Ma M; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA., Theobald N; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA., Burkett S; Molecular Cytogenetic Core Facility, Mouse Cancer Genetics Program, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Frederick, MD 21702, USA., Sweeney CL; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA., Lazzarotto CR; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN 38105, USA., Lack JB; Bioinformatics (NCBR)/Integrated Data Sciences Section (IDSS), Research Technology Branch/DIR/NIAID, Frederick, MD 21702, USA., Wu X; Molecular Cytogenetic Core Facility, Mouse Cancer Genetics Program, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Frederick, MD 21702, USA., Dahl GA; CELLSCRIPT, Madison, WI 53713, USA.; Wisconsin Institute for Immune and Cell Therapy (WIICT), Madison, WI 53713, USA., Malech HL; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA., Kleinstiver BP; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA 02114, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA 02114, USA.; Department of Pathology, Harvard Medical School, Boston, MA 02115, USA., De Ravin SS; Genetic Immunotherapy Section, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD 20892, USA.
Publikováno v:
Science translational medicine [Sci Transl Med] 2024 Oct 16; Vol. 16 (769), pp. eadj6779. Date of Electronic Publication: 2024 Oct 16.
Autor:
Katta V; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., O'Keefe K; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Li Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Mayuranathan T; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Lazzarotto CR; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Wood RK; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Levine RM; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Powers A; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Mayberry K; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Manquen G; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Yao Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Zhang J; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Jang Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Nimmagadda N; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Dempsey EA; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Lee G; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Uchida N; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute/National Institute of Diabetes and Digestive and Kidney Diseases, National Institute of Health Bethesda, Bethesda, MD, USA., Cheng Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Fazio F; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Lockey T; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Meagher M; Children's GMP LLC, St. Jude Children's Research Hospital, Memphis, TN, USA., Sharma A; Department of Bone Marrow Transplantation & Cellular Therapy, St. Jude Children's Research Hospital, Memphis, TN, USA., Tisdale JF; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute/National Institute of Diabetes and Digestive and Kidney Diseases, National Institute of Health Bethesda, Bethesda, MD, USA., Zhou S; Experimental & Cellular Therapeutics Lab, St. Jude Children's Research Hospital, Memphis, TN, USA., Yen JS; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: jonathan.yen@stjude.org., Weiss MJ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: mitch.weiss@stjude.org., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. Electronic address: shengdar.tsai@stjude.org.
Publikováno v:
Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2024 Oct 02; Vol. 32 (10), pp. 3433-3452. Date of Electronic Publication: 2024 Jul 31.
Autor:
Garaudé S; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Marone R; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Lepore R; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland.; Cimeio Therapeutics, Basel, Switzerland., Devaux A; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Beerlage A; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland.; Department of Hematology, Basel University Hospital, Basel, Switzerland., Seyres D; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Dell' Aglio A; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Juskevicius D; Department of Laboratory Medicine, Diagnostic Hematology, Basel University Hospital, Basel, Switzerland., Zuin J; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Burgold T; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland., Wang S; Division of Hematology, Department of Oncology, Geneva University Hospitals, Geneva, Switzerland., Katta V; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Manquen G; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Li Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Larrue C; Translational Research Center for Oncohematology, Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland.; Centre de Recherches en Cancérologie de Toulouse, Université de Toulouse, Inserm, CNRS, Toulouse, France., Camus A; Cimeio Therapeutics, Basel, Switzerland., Durzynska I; Ridgeline Discovery, Basel, Switzerland., Wellinger LC; Ridgeline Discovery, Basel, Switzerland., Kirby I; ADC Therapeutics (UK), London, UK., Van Berkel PH; ADC Therapeutics (UK), London, UK., Kunz C; Ridgeline Discovery, Basel, Switzerland., Tamburini J; Translational Research Center for Oncohematology, Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland., Bertoni F; Institute of Oncology Research, Faculty of Biomedical Sciences, USI, Bellinzona, Switzerland.; Oncology Institute of Southern Switzerland, Ente Ospedaliero Cantonale, Bellinzona, Switzerland., Widmer CC; Department of Hematology, Basel University Hospital, Basel, Switzerland.; Department of Laboratory Medicine, Diagnostic Hematology, Basel University Hospital, Basel, Switzerland., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Simonetta F; Division of Hematology, Department of Oncology, Geneva University Hospitals, Geneva, Switzerland.; Translational Research Center for Oncohematology, Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland., Urlinger S; Cimeio Therapeutics, Basel, Switzerland., Jeker LT; Department of Biomedicine, Basel University Hospital and University of Basel, Basel, Switzerland. lukas.jeker@unibas.ch.; Transplantation Immunology & Nephrology, Basel University Hospital, Basel, Switzerland. lukas.jeker@unibas.ch.; Innovation Focus Cell Therapy, Basel University Hospital, Basel, Switzerland. lukas.jeker@unibas.ch.
Publikováno v:
Nature [Nature] 2024 Jun; Vol. 630 (8017), pp. 728-735. Date of Electronic Publication: 2024 May 22.
Publikováno v:
BioRxiv : the preprint server for biology [bioRxiv] 2024 Mar 30. Date of Electronic Publication: 2024 Mar 30.
Publikováno v:
BioRxiv : the preprint server for biology [bioRxiv] 2024 Feb 14. Date of Electronic Publication: 2024 Feb 14.
Autor:
Alves CRR; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA. calves2@mgh.harvard.edu.; Department of Neurology, Massachusetts General Hospital, Boston, MA, USA. calves2@mgh.harvard.edu.; Department of Neurology, Harvard Medical School, Boston, MA, USA. calves2@mgh.harvard.edu., Ha LL; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA., Yaworski R; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Sutton ER; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Lazzarotto CR; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Christie KA; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Harvard Medical School, Boston, MA, USA., Reilly A; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Beauvais A; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada., Doll RM; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA.; Molecular Biosciences/Cancer Biology Program, Heidelberg University and German Cancer Research Center (DKFZ), Heidelberg, Germany., de la Cruz D; Molecular Neurogenetics Unit, Department of Neurology, Massachusetts General Hospital, Charlestown, MA, USA.; Program in Neuroscience, Harvard Medical School, Boston, MA, USA., Maguire CA; Molecular Neurogenetics Unit, Department of Neurology, Massachusetts General Hospital, Charlestown, MA, USA.; Program in Neuroscience, Harvard Medical School, Boston, MA, USA., Swoboda KJ; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA.; Department of Neurology, Massachusetts General Hospital, Boston, MA, USA.; Department of Neurology, Harvard Medical School, Boston, MA, USA., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Kothary R; Ottawa Hospital Research Institute, Ottawa, Ontario, Canada.; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa, Ontario, Canada.; Centre for Neuromuscular Disease, University of Ottawa, Ottawa, Ontario, Canada.; Department of Medicine, University of Ottawa, Ottawa, Ontario, Canada., Kleinstiver BP; Center for Genomic Medicine, Massachusetts General Hospital, Boston, MA, USA. bkleinstiver@mgh.harvard.edu.; Department of Pathology, Massachusetts General Hospital, Boston, MA, USA. bkleinstiver@mgh.harvard.edu.; Department of Pathology, Harvard Medical School, Boston, MA, USA. bkleinstiver@mgh.harvard.edu.
Publikováno v:
Nature biomedical engineering [Nat Biomed Eng] 2024 Feb; Vol. 8 (2), pp. 118-131. Date of Electronic Publication: 2023 Dec 06.
Autor:
Cavazza A; Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child Health, University College London, WC1N 1EH London, UK., Hendel A; Institute of Nanotechnology and Advanced Materials, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat-Gan 52900, Israel., Bak RO; Department of Biomedicine, Aarhus University, 8000 Aarhus C, Denmark., Rio P; Hematopoietic Innovative Therapies Division, Centro de Investigaciones Energéticas Medioambientales y Tecnológicas and Centro de Investigación Biomédica en Red de Enfermedades Raras (CIEMAT/CIBERER), 28040 Madrid, Spain.; Advanced Therapies Unit, Instituto de Investigación Sanitaria Fundación Jiménez Díaz (IIS-FJD, UAM), 28040 Madrid, Spain., Güell M; Department of Medicine and Life Sciences, Universitat Pompeu Fabra, Barcelona, Spain.; Integra Therapeutics S.L., Barcelona, Spain., Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia., Arechavala-Gomeza V; Nucleic Acid Therapeutics for Rare Disorders (NAT-RD), Biobizkaia Health Research Institute, Barakaldo, Spain.; Ikerbasque, Basque Foundation for Science, Bilbao, Spain., Peng L; Aix Marseille University, CNRS, Centre Interdisciplinaire de Nanoscience de Marseille, UMR 7325, Equipe Labellisée Ligue Contre le Cancer, 13288 Marseille, France., Hapil FZ; Department of Medical Biology and Genetics, Faculty of Medicine, Akdeniz University, Antalya, Turkey., Harvey J; Institute of Ophthalmology, University College London, London, UK., Ortega FG; GENYO, Centre for Genomics and Oncological Research, Pfizer/University of Granada/Andalusian Regional Government, Avenida de la Ilustración 114, 18016 Granada, Spain.; IBS Granada, Institute of Biomedical Research, Avenida de Madrid 15, 18012 Granada, Spain., Gonzalez-Martinez C; GENYO, Centre for Genomics and Oncological Research, Pfizer/University of Granada/Andalusian Regional Government, Avenida de la Ilustración 114, 18016 Granada, Spain.; IBS Granada, Institute of Biomedical Research, Avenida de Madrid 15, 18012 Granada, Spain., Lederer CW; Department of Molecular Genetics Thalassaemia, The Cyprus Institute of Neurology and Genetics, Nicosia, Cyprus., Mikkelsen K; Department of Biomedicine, Aarhus University, 8000 Aarhus C, Denmark., Gasiunas G; CasZyme, 10224 Vilnius, Lithuania., Kalter N; Institute of Nanotechnology and Advanced Materials, The Mina and Everard Goodman Faculty of Life Sciences, Bar-Ilan University, Ramat-Gan 52900, Israel., Gonçalves MAFV; Department of Cell and Chemical Biology, Leiden University Medical Center, Einthovenweg 20, 2333 ZC Leiden, the Netherlands., Petersen J; Steno Diabetes Center Aarhus, Aarhus University Hospital, 8200 Aarhus N, Denmark., Garanto A; Department of Pediatrics and Department of Human Genetics, Amalia Children's Hospital, Radboud University Medical Center, Nijmegen, the Netherlands., Montoliu L; Department of Molecular and Cellular Biology, National Centre for Biotechnology (CNB-CSIC) and Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER-ISCIII), Madrid, Spain., Maresca M; Genome Engineering, Discovery Sciences, BioPharmaceuticals R&D Unit, AstraZeneca, Gothenburg, Sweden., Seemann SE; Center for Non-coding RNA in Technology and Health, Department of Veterinary and Animal Sciences, University of Copenhagen, Copenhagen, Denmark., Gorodkin J; Center for Non-coding RNA in Technology and Health, Department of Veterinary and Animal Sciences, University of Copenhagen, Copenhagen, Denmark., Mazini L; Laboratory of Genetic Engineering, Technologic, Medical and Academic Park (TMAP), Marrakech, Morocco., Sanchez R; GENYO, Centre for Genomics and Oncological Research, Pfizer/University of Granada/Andalusian Regional Government, PTS Granada, Granada, Spain.; Department of Medicinal & Organic Chemistry and Excellence Research Unit of 'Chemistry Applied to Biomedicine and the Environment,' Faculty of Pharmacy, University of Granada, Campus de Cartuja s/n, Granada, Spain.; Instituto de Investigación Biosanitaria de Granada (ibs.GRANADA), Universidad de Granada, Granada, Spain., Rodriguez-Madoz JR; Cancer Center Clinica Universidad de Navarra (CCUN), Pamplona, Spain.; Instituto de Investigación Sanitaria de Navarra (IdiSNA), Pamplona, Spain.; Centro de Investigación Biomédica en Red de Cancer (CIBERONC), Madrid, Spain., Maldonado-Pérez N; Steno Diabetes Center Aarhus, Aarhus University Hospital, 8200 Aarhus N, Denmark., Laura T; DNA & RNA Medicine Division, Center for Applied Medical Research (CIMA) Universidad de Navarra, 31008 Pamplona, Spain., Schmueck-Henneresse M; Berlin Institute for Health (BIH) at Charité - Universitätsmedizin Berlin, BIH Center for Regenerative Therapies (BCRT), Charitéplatz 1, 10117 Berlin, Germany., Maccalli C; Laboratory of Immune Biological Therapy, Research Branch, Sidra Medicine, PO Box 26999, Doha, Qatar., Grünewald J; Department of Medicine, Cardiology, Angiology, Pneumology, Klinikum rechts der Isar, Technical University of Munich, TUM School of Medicine and Health, TranslaTUM, MIBE, Munich, Germany.; Center for Organoid Systems, Munich, Germany., Carmona G; Red Andaluza de diseño y traslación de Terapias Avanzadas-RAdytTA, Fundación Pública Andaluza Progreso y Salud-FPS, Sevilla, España., Kachamakova-Trojanowska N; Malopolska Centre of Biotechnology, Jagiellonian University, 30-387 Krakow, Poland., Miccio A; Imagine Institute, Laboratory of Chromatin and Gene Regulation During Development, Université de Paris Cité, INSERM UMR 1163, 75015 Paris, France., Martin F; Bioquímica y Biología Molecular III e Immunology Department, Facultad de Medicina, Universidad de Granada and Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), PTS, Av. de la Ilustración 114, 18016 Granada, Spain., Turchiano G; Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child Health, University College London, WC1N 1EH London, UK., Cathomen T; Institute for Transfusion Medicine and Gene Therapy, Medical Center-University of Freiburg, Freiburg, Germany.; Medical Faculty, University of Freiburg, 79106 Freiburg, Germany., Luo Y; Department of Biomedicine, Aarhus University, 8000 Aarhus C, Denmark.; Steno Diabetes Center Aarhus, Aarhus University Hospital, 8200 Aarhus N, Denmark., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Benabdellah K; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), PTS, Av. de la Ilustración 114, 18016 Granada, Spain.
Publikováno v:
Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2023 Oct 29; Vol. 34, pp. 102066. Date of Electronic Publication: 2023 Oct 29 (Print Publication: 2023).
Autor:
Molugu K; Biophysics Graduate Program, University of Wisconsin-Madison, Madison, Wisconsin, USA; St Jude Children's Research Hospital, Memphis, Tennessee, USA.; Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, Wisconsin, USA; St Jude Children's Research Hospital, Memphis, Tennessee, USA., Khajanchi N; Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, Wisconsin, USA; St Jude Children's Research Hospital, Memphis, Tennessee, USA.; Department of Biomedical and Engineering, University of Wisconsin-Madison, Madison, Wisconsin, USA; and St Jude Children's Research Hospital, Memphis, Tennessee, USA., Lazzarotto CR; Department of Hematology, St Jude Children's Research Hospital, Memphis, Tennessee, USA., Tsai SQ; Department of Hematology, St Jude Children's Research Hospital, Memphis, Tennessee, USA., Saha K; Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, Wisconsin, USA; St Jude Children's Research Hospital, Memphis, Tennessee, USA.; Department of Biomedical and Engineering, University of Wisconsin-Madison, Madison, Wisconsin, USA; and St Jude Children's Research Hospital, Memphis, Tennessee, USA.
Publikováno v:
The CRISPR journal [CRISPR J] 2023 Oct; Vol. 6 (5), pp. 473-485. Date of Electronic Publication: 2023 Sep 07.
Autor:
Mayuranathan T; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Newby GA; Merkin Institute of Transformative Technologies in Healthcare, Broad Institute of Harvard and MIT, Cambridge, MA, USA.; Department of Chemistry and Chemical Biology, Harvard University, Cambridge, MA, USA.; Howard Hughes Medical Institute, Harvard University, Cambridge, MA, USA., Feng R; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Yao Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Mayberry KD; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Lazzarotto CR; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Li Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Levine RM; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Nimmagadda N; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Dempsey E; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Kang G; Department of Biostatistics, St. Jude Children's Research Hospital, Memphis, TN, USA., Porter SN; Department of Cell and Molecular Biology, St. Jude Children's Research Hospital, Memphis, TN, USA., Doerfler PA; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Zhang J; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Jang Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Chen J; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Bell HW; School of Biotechnology and Biomolecular Sciences, University of New South Wales, Sydney, New South Wales, Australia., Crossley M; School of Biotechnology and Biomolecular Sciences, University of New South Wales, Sydney, New South Wales, Australia., Bhoopalan SV; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Sharma A; Department of Bone Marrow Transplantation and Cellular Therapy, St. Jude Children's Research Hospital, Memphis, TN, USA., Tisdale JF; Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute and National Institute of Diabetes and Digestive and Kidney Diseases, Bethesda, MD, USA., Pruett-Miller SM; Department of Cell and Molecular Biology, St. Jude Children's Research Hospital, Memphis, TN, USA., Cheng Y; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Tsai SQ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA., Liu DR; Merkin Institute of Transformative Technologies in Healthcare, Broad Institute of Harvard and MIT, Cambridge, MA, USA. drliu@fas.harvard.edu.; Department of Chemistry and Chemical Biology, Harvard University, Cambridge, MA, USA. drliu@fas.harvard.edu.; Howard Hughes Medical Institute, Harvard University, Cambridge, MA, USA. drliu@fas.harvard.edu., Weiss MJ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. mitch.weiss@stjude.org., Yen JS; Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN, USA. jonathan.yen@stjude.org.
Publikováno v:
Nature genetics [Nat Genet] 2023 Jul; Vol. 55 (7), pp. 1210-1220. Date of Electronic Publication: 2023 Jul 03.