Safety and effectiveness of taliglucerase alfa in patients with Gaucher disease: an interim analysis of real-world data from a multinational drug registry (TALIAS)

Autor: Lina Titievsky, Tilman Schuster, Ronnie Wang, Muhammad Younus, Andrew Palladino, Kabir Quazi, Michael P. Wajnrajch, Betina Hernandez, Pamela S. Becker, Neal J. Weinreb, Christina Chambers, Roy Mansfield, Louise Taylor, Li-Jung Tseng, Paige Kaplan

Publikováno v: Orphanet Journal of Rare Diseases, Vol 17, Iss 1, Pp 1-11 (2022)

Abstract Background Limited real-world data from routine clinical care are available on the safety and effectiveness of treatment with taliglucerase alfa in patients with Gaucher disease (GD). Methods Taliglucerase Alfa Surveillance (TALIAS), a multi

Externí odkaz: https://doaj.org/article/a2312ba99d1246d0b5b5524f11be215f

Safety and effectiveness of taliglucerase alfa in patients with Gaucher disease: an interim analysis of real-world data from a multinational drug registry (TALIAS).

Autor: Titievsky, Lina¹ (AUTHOR), Schuster, Tilman¹ (AUTHOR), Wang, Ronnie¹ (AUTHOR), Younus, Muhammad² (AUTHOR) Muhammad.Younus2@pfizer.com, Palladino, Andrew¹ (AUTHOR), Quazi, Kabir¹ (AUTHOR), Wajnrajch, Michael P.^1,3 (AUTHOR), Hernandez, Betina¹ (AUTHOR), Becker, Pamela S.^4,5 (AUTHOR), Weinreb, Neal J.⁶ (AUTHOR), Chambers, Christina⁷ (AUTHOR), Mansfield, Roy¹ (AUTHOR), Taylor, Louise¹ (AUTHOR), Tseng, Li-Jung¹ (AUTHOR), Kaplan, Paige⁸ (AUTHOR)

Publikováno v: Orphanet Journal of Rare Diseases. 4/1/2022, Vol. 17 Issue 1, p1-11. 11p.