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of 2
pro vyhledávání: '"Tatianna W Y Wong"'
Targeted genome editing in vivo corrects a Dmd duplication restoring wild‐type dystrophin expression
Autor:
Eleonora Maino, Daria Wojtal, Sonia L Evagelou, Aiman Farheen, Tatianna W Y Wong, Kyle Lindsay, Ori Scott, Samar Z Rizvi, Elzbieta Hyatt, Matthew Rok, Shagana Visuvanathan, Amanda Chiodo, Michelle Schneeweiss, Evgueni A Ivakine, Ronald D Cohn
Publikováno v:
EMBO Molecular Medicine, Vol 13, Iss 5, Pp 1-15 (2021)
Abstract Tandem duplication mutations are increasingly found to be the direct cause of many rare heritable diseases, accounting for up to 10% of cases. Unfortunately, animal models recapitulating such mutations are scarce, limiting our ability to stu
Externí odkaz:
https://doaj.org/article/79b8670d90524c9f9b3d247d4ec1653b
Autor:
Suja Shrestha, Meghan J. McFadden, Allen C. T. Teng, Patrick Dong Min Chang, Joyce Deng, Tatianna W. Y. Wong, Ronald D. Cohn, Evgueni A. Ivakine, Anthony O. Gramolini, J. Paul Santerre
Publikováno v:
ACS Applied Materials & Interfaces. 13:58352-58368
Developing safe and effective strategies to deliver biomolecules such as oligonucleotides and proteins into cells has grown in importance over recent years, with an increasing demand for non-viral methods that enable clinical translation. Here, we in
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::263f013586bb0dd551cd3774b30b5414
https://doi.org/10.1021/acsami.1c17868
https://doi.org/10.1021/acsami.1c17868