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pro vyhledávání: '"Susan M Tuominen"'
Autor:
Stephanie G Bertrand, Mohammed Salman Shazeeb, Erin Horn, Deborah Fernau, Miguel Sena-Esteves, Toloo Taghian, Lindsey J Bierfeldt, Aly Abayazeed, Oguz Cataltepe, Stephen Frey, Susan M Tuominen, Jennifer W. Koehler, Heather L. Gray-Edwards, Terence R. Flotte, Matthew J. Gounis
Publikováno v:
Human Gene Therapy. 31:617-625
Thalamic infusion of adeno-associated viral (AAV) vectors has been shown to have therapeutic effects in neuronopathic lysosomal storage diseases. Preclinical studies in sheep model of Tay-Sachs disease demonstrated that bilateral thalamic injections
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::96d84109bf74c289d2790f00cbf8260a
https://doi.org/10.1089/hum.2019.288
https://doi.org/10.1089/hum.2019.288
