Zobrazeno 1 - 9
of 9
pro vyhledávání: '"Sueli Canossa"'
Autor:
Sandra Obikawa Kyosen, Leny Toma, Helena Bonciani Nader, Marion Coting Braga, Vanessa Gonçalves Pereira, Sueli Canossa, João Bosco Pesquero, Vânia D’Almeida, Ana Maria Martins
Publikováno v:
Revista Paulista de Pediatria, Iss 0 (2019)
ABSTRACT Objective: To report the stabilization of urinary glycosaminoglicans (GAG) excretion and clinical improvements in patients with mucopolysaccharidosis type I (MPS I) under an alternative dose regimen of laronidase of 1.2 mg/kg every other wee
Externí odkaz:
https://doaj.org/article/38637534098d49dc82dca4878f97d736
Autor:
Helena B. Nader, Marion Coting Braga, Vânia D'Almeida, Sandra Obikawa Kyosen, João Bosco Pesquero, Ana Maria Martins, Leny Toma, Vanessa Gonçalves Pereira, Sueli Canossa
Publikováno v:
Revista Paulista de Pediatria, Iss 0 (2019)
Revista Paulista de Pediatria v.37 n.3 2019
Revista Paulista de Pediatria (Ed. Português. Online)
Sociedade de Pediatria de São Paulo (SPSP)
instacron:SPSP
Revista Paulista de Pediatria
Revista Paulista de Pediatria v.37 n.3 2019
Revista Paulista de Pediatria (Ed. Português. Online)
Sociedade de Pediatria de São Paulo (SPSP)
instacron:SPSP
Revista Paulista de Pediatria
Objective: To report the stabilization of urinary glycosaminoglicans (GAG) excretion and clinical improvements in patients with mucopolysaccharidosis type I (MPS I) under an alternative dose regimen of laronidase of 1.2 mg/kg every other week. Method
Autor:
Maria Lúcia Costa de Oliveira, Anneliese Lopes Barth, Fernanda B. Scalco, Carolina Fischinger Moura de Souza, Sandra Obikawa Kyosen, Ana Maria Martins, Dafne Dain Gandelman Horovitz, Sueli Canossa, Marco A. Curiati
Publikováno v:
Molecular Genetics and Metabolism. 126:S74-S75
Enzyme replacement therapy for mucopolysaccharidosis II (MPS II) with Idursulfase (ElapraseR) has proven effective in reducing urinary glycosaminoglycan (uGAG) levels, liver and spleen volumes and in increasing walking distance. During phase II/III s
Autor:
Rosângela M, Silva, Carmen S C, Mendes, Carolina C, Aranda, Marco A, Curiati, Maret H, Rand, Sandra O, Kyosen, Edna T, Sakata, Sueli, Canossa, Renata B, Oliveira, Ana M, Martins
Publikováno v:
Journal of neuromuscular diseases. 2(s1)
Autor:
Inês Cristina Camelo Nunes, Ekaterine S. Goudouris, Dirceu Solé, Carolina Sanchez Aranda, Marcia C. Mallozi, Luis Felipe Ensina, Ana Maria Martins, Sueli Canossa
Publikováno v:
Journal of Allergy and Clinical Immunology. 139:AB42
Autor:
Ana Maria Martins, Maret H. Rand, Renata B. Oliveira, Cintia M. Goncalves, Sandra Obikawa Kyosen, Carolina Sanchez Aranda, Marco A. Curiati, Carmen Mendes, Rosangela Maria Silva, Sueli Canossa, J. R. P. Silva
Publikováno v:
Molecular Genetics and Metabolism. 114:S34-S35
Autor:
Sandra Obikawa Kyosen, Rosângela M Silva, Ana Maria Martins, Edna Tiemi, Sueli Canossa, C.L. Patti, Carmen Mendes
Publikováno v:
Molecular Genetics and Metabolism. 114:S106
Physical exercise is important for promoting health and improving quality of life; however, patients with lysosomal disease (LSD) usually present exercise intolerance characterized by low fitness; therefore, exercise should be prescribed individually
Autor:
Rosângela M Silva, Sueli Canossa, Sandra Obikawa Kyosen, Ana Maria Martins, Carolina C Aranda, Marco A. Curiati, Maret H. Rand, Edna Tiemi Sakata, Renata B. Oliveira, Carmen Mendes
Publikováno v:
Journal of Neuromuscular Diseases. 2:S33-S33
Pompe disease (PD) causes a progressive muscular weakness and impairment of patients’ mobility. Many patients develop intolerance to exercise due to reduced activity and consequent decline in muscle function. Exercise training prevents physical dec
Autor:
Sandra Obikawa Kyosen, Marco A. Curiati, Beatriz Jurkiewcz Frangipani, Carmen Mendes, Carolina C Aranda, Maret H. Rand, Edna Tiemi Sakata, Sueli Canossa, Ana Maria Martins, Rosângela M Silva
Publikováno v:
Journal of Neuromuscular Diseases. 2:S32-S32
Pompe disease is a progressive multisystem disease caused by a lysosomal acid α-glycosidase enzyme (GAA) defi ciency, resulting in lysosomal accumulation of glycogen. The late-onset form is characterized by progressive skeletal and respiratory muscl