Zobrazeno 1 - 10
of 222
pro vyhledávání: '"Steven W. Pipe"'
Autor:
Flora Peyvandi, David Lillicrap, Johnny Mahlangu, Claire McLintock, K. John Pasi, Steven W. Pipe, Wendy Scales, Alok Srivastava, Thierry VandenDriessche
Publikováno v:
Research and Practice in Thrombosis and Haemostasis, Vol 4, Iss 4, Pp 644-651 (2020)
Abstract Background Hemophilia gene therapy is a rapidly evolving therapeutic approach in which a number of programs are approaching clinical development completion. Objective The aim of this study was to evaluate knowledge and perceptions of a varie
Externí odkaz:
https://doaj.org/article/c1ff5ac1480648eb8dbeb547ea1ccccd
Autor:
Annette Von Drygalski, Adam Giermasz, Giancarlo Castaman, Nigel S. Key, Susan Lattimore, Frank W.G. Leebeek, Wolfgang Miesbach, Michael Recht, Alison Long, Robert Gut, Eileen K. Sawyer, Steven W. Pipe
Publikováno v:
Blood Advances, Vol 3, Iss 21, Pp 3241-3247 (2019)
Etranacogene dezaparvovec (AMT-061) is a recombinant AAV5 vector including a gene cassette containing the factor IX (FIX) Padua variant under the control of a liver-specific promoter. A phase 2b study was conducted to confirm that a single dose of 2
Externí odkaz:
https://doaj.org/article/66cb66c72e9147b78eee95d74a7a1df4
Publikováno v:
Blood Advances, Vol 3, Iss 18, Pp 2748-2750 (2019)
Externí odkaz:
https://doaj.org/article/2f8325906470489893a81ccaf115f802
Autor:
Einas Elsheikh, Michelle Lavin, Lilian Antunes Heck, Niamh Larkin, Brendan Mullaney, Dearbhla Doherty, Megan Kennedy, Catriona Keenan, Thomas Guest, Brian O'Mahony, Judicael Fazavana, Padraic G. Fallon, Roger J.S. Preston, John Gormley, Kevin Ryan, Niamh M. O'Connell, Evelyn Singleton, Mary Byrne, Mark McGowan, Sheila Roche, Mairead Doyle, Maeve P. Crowley, Susan I. O'Shea, Birgit M. Reipert, Jill M. Johnsen, Steven W. Pipe, Jorge Di Paola, Peter L. Turecek, James S. O'Donnell
Publikováno v:
Journal of Thrombosis and Haemostasis. 21:1123-1134
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::466954f23f25d68ab01a21abab4d5434
https://doi.org/10.1016/j.jtha.2023.01.013
https://doi.org/10.1016/j.jtha.2023.01.013
Autor:
Alok Srivastava, Savita Rangarajan, Kaan Kavakli, Robert Klamroth, Gili Kenet, Liane Khoo, Chur-Woo You, Weiqun Xu, Niel Malan, Laurent Frenzel, Catherine N Bagot, Oleksandra Stasyshyn, Chia-Yau Chang, Stacey Poloskey, Zhiying Qiu, Shauna Andersson, Baisong Mei, Steven W Pipe
Publikováno v:
The Lancet Haematology. 10:e322-e332
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::69e0609c06dd026ce31292efb0be346b
https://doi.org/10.1016/s2352-3026(23)00037-6
https://doi.org/10.1016/s2352-3026(23)00037-6
Autor:
Margaret V. Ragni, Guy Young, Glaivy Batsuli, Emily Bisson, Shannon L. Carpenter, Stacy E. Croteau, Adam Cuker, Randall G. Curtis, Michael Denne, Bruce Ewenstein, Amber Federizo, Neil Frick, Kerry Funkhouser, Lindsey A. George, W. Keith Hoots, Shawn M. Jobe, Emily Krava, Christopher James Langmead, Roger J. Lewis, José López, Lynn Malec, Ziva Mann, Moses E. Miles, Emma Neely, Ellis J. Neufeld, Glenn F. Pierce, Steven W. Pipe, Lisa R. Pitler, Leslie Raffini, Kathaleen M. Schnur, Jordan A. Shavit
Publikováno v:
Expert Review of Hematology. 16:107-127
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::60465e8fcb91f7f8234e18e9dbcab6f8
https://doi.org/10.1080/17474086.2023.2181781
https://doi.org/10.1080/17474086.2023.2181781
Autor:
Steven W. Pipe, Frank W.G. Leebeek, Michael Recht, Nigel S. Key, Giancarlo Castaman, Wolfgang Miesbach, Susan Lattimore, Kathelijne Peerlinck, Paul Van der Valk, Michiel Coppens, Peter Kampmann, Karina Meijer, Niamh O’Connell, K. John Pasi, Daniel P. Hart, Rashid Kazmi, Jan Astermark, Cedric R.J.R. Hermans, Robert Klamroth, Richard Lemons, Nathan Visweshwar, Annette von Drygalski, Guy Young, Shelley E. Crary, Miguel Escobar, Esteban Gomez, Rebecca Kruse-Jarres, Doris V. Quon, Emily Symington, Michael Wang, Allison P. Wheeler, Robert Gut, Ying P. Liu, Ricardo E. Dolmetsch, David L. Cooper, Yanyan Li, Brahm Goldstein, Paul E. Monahan
Publikováno v:
New England journal of medicine, 388(8), 706-718. Massachussetts Medical Society
New England Journal of Medicine, 388(8), 706-718. MASSACHUSETTS MEDICAL SOC
New England Journal of Medicine, 388(8), 706-718. Massachussetts Medical Society
New England Journal of Medicine, 388(8), 706-718. MASSACHUSETTS MEDICAL SOC
New England Journal of Medicine, 388(8), 706-718. Massachussetts Medical Society
Background: Moderate-to-severe hemophilia B is treated with lifelong, continuous coagulation factor IX replacement to prevent bleeding. Gene therapy for hemophilia B aims to establish sustained factor IX activity, thereby protecting against bleeding
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::18ec00c53efc81770ed02e6372363e8b
https://hdl.handle.net/11370/bcd8e7fb-66c2-4b0f-b235-d2995c4d444f
https://hdl.handle.net/11370/bcd8e7fb-66c2-4b0f-b235-d2995c4d444f
Autor:
Steven W. Pipe
Publikováno v:
Blood. 140:2650-2652
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9403f8f9f9ab7ff87a493f3069bb11b9
https://doi.org/10.1182/blood.2022016359
https://doi.org/10.1182/blood.2022016359
Publikováno v:
Expert Opinion on Biological Therapy. 22:1091-1098
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::7662ca065adc8d17d115e8b6acea9280
https://doi.org/10.1080/14712598.2022.2090241
https://doi.org/10.1080/14712598.2022.2090241
Autor:
Steven W. Pipe, Frank W.G. Leebeek, Michael Recht, Nigel S. Key, Susan Lattimore, Giancarlo Castaman, David Cooper, Stephanie Verweij, Ricardo Dolmetsch, Jacqueline Tarrant, Yanyan Li, Paul E. Monahan, Wolfgang A. Miesbach
Publikováno v:
Blood. 140:4904-4906
Externí odkaz:
https://explore.openaire.eu/search/publication?articleId=doi_________::773f2c6ceb630a843b1d82a97c8d0f35
https://doi.org/10.1182/blood-2022-166745
https://doi.org/10.1182/blood-2022-166745